Publications (6)

¹ Publicaciones consideradas como producción del grupo

filter_list Drug Discovery

2023

  1. Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides

    Nucleic acid therapeutics, Vol. 33, Núm. 1, pp. 1-16

  2. Experimental Model Systems Used in the Preclinical Development of Nucleic Acid Therapeutics

    Nucleic Acid Therapeutics, Vol. 33, Núm. 4, pp. 238-247

2022

  1. Antisense RNA Therapeutics: A Brief Overview

    Methods in Molecular Biology (Humana Press Inc.), pp. 33-49

  2. Lessons learned from developing an oligonucleotide drug for a rare disease

    RNA Therapeutics: The Evolving Landscape of RNA Therapeutics (Elsevier), pp. 121-137

2021

  1. Delivery of oligonucleotide-based therapeutics: challenges and opportunities

    EMBO Molecular Medicine, Vol. 13, Núm. 4

2017

  1. Delivery is key: lessons learnt from developing splice-switching antisense therapies

    EMBO Molecular Medicine, Vol. 9, Núm. 5, pp. 545-557