In vitro correction of a pseudoexon-generating deep intronic mutation in LGMD2A by antisense oligonucleotides and modified small nuclear RNAs

1. Blázquez, L.
2. Aiastui, A.
3. Goicoechea, M.
4. Martins de Araujo, M.
5. Avril, A.
6. Beley, C.
7. García, L.
8. Valcárcel, J.
9. Fortes, P.
10. López de Munain, A.