International best practice for the evaluation of responsiveness to sapropterin dihydrochloride in patients with phenylketonuria

  1. Muntau, A.C.
  2. Adams, D.J.
  3. Bélanger-Quintana, A.
  4. Bushueva, T.V.
  5. Cerone, R.
  6. Chien, Y.-H.
  7. Chiesa, A.
  8. Coşkun, T.
  9. de las Heras, J.
  10. Feillet, F.
  11. Katz, R.
  12. Lagler, F.
  13. Piazzon, F.
  14. Rohr, F.
  15. van Spronsen, F.J.
  16. Vargas, P.
  17. Wilcox, G.
  18. Bhattacharya, K.
Journal:
Molecular Genetics and Metabolism

ISSN: 1096-7206,  1096-7192

Year of publication: 2019

Volume: 127

Issue: 1

Pages: 1-11

Type: Review

DOI: 10.1016/J.YMGME.2019.04.004 GOOGLE SCHOLAR lock_openOpen access editor

Sustainable development goals

Data source: Scopus