Why dystrophin quantification is key in the eteplirsen saga

  1. Aartsma-Rus, A.
  2. Arechavala-Gomeza, V.
Revue:
Nature reviews. Neurology

ISSN: 1759-4766

Année de publication: 2018

Volumen: 14

Número: 8

Pages: 454-456

Type: Note

DOI: 10.1038/S41582-018-0033-8 GOOGLE SCHOLAR

Objectifs de Développement Durable