Delivery is key: lessons learnt from developing splice-switching antisense therapies

  1. Godfrey, C.
  2. Desviat, L.R.
  3. Smedsrød, B.
  4. Piétri-Rouxel, F.
  5. Denti, M.A.
  6. Disterer, P.
  7. Lorain, S.
  8. Nogales-Gadea, G.
  9. Sardone, V.
  10. Anwar, R.
  11. El Andaloussi, S.
  12. Lehto, T.
  13. Khoo, B.
  14. Brolin, C.
  15. van Roon-Mom, W.M.C.
  16. Goyenvalle, A.
  17. Aartsma-Rus, A.
  18. Arechavala-Gomeza, V.
Journal:
EMBO Molecular Medicine

ISSN: 1757-4684,  1757-4676

Year of publication: 2017

Volume: 9

Issue: 5

Pages: 545-557

Type: Review

DOI: 10.15252/EMMM.201607199 GOOGLE SCHOLAR lock_openOpen access editor

Sustainable development goals

Data source: Scopus