Stakeholder cooperation to overcome challenges in orphan medicine development: The example of Duchenne muscular dystrophy

1. Straub, V.
2. Balabanov, P.
3. Bushby, K.
4. Ensini, M.
5. Goemans, N.
6. De Luca, A.
7. Pereda, A.
8. Hemmings, R.
9. Campion, G.
10. Kaye, E.
11. Arechavala-Gomeza, V.
12. Goyenvalle, A.
13. Niks, E.
14. Veldhuizen, O.
15. Furlong, P.
16. Stoyanova-Beninska, V.
17. Wood, M.J.
18. Johnson, A.
19. Mercuri, E.
20. Muntoni, F.
21. Sepodes, B.
22. Haas, M.
23. Vroom, E.
24. Aartsma-Rus, A.