Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

  1. Kinali, M.
  2. Arechavala-Gomeza, V.
  3. Feng, L.
  4. Cirak, S.
  5. Hunt, D.
  6. Adkin, C.
  7. Guglieri, M.
  8. Ashton, E.
  9. Abbs, S.
  10. Nihoyannopoulos, P.
  11. Garralda, M.E.
  12. Rutherford, M.
  13. Mcculley, C.
  14. Popplewell, L.
  15. Graham, I.R.
  16. Dickson, G.
  17. Wood, M.J.
  18. Wells, D.J.
  19. Wilton, S.D.
  20. Kole, R.
  21. Straub, V.
  22. Bushby, K.
  23. Sewry, C.
  24. Morgan, J.E.
  25. Muntoni, F.
Revue:
The Lancet Neurology

ISSN: 1474-4422

Année de publication: 2009

Volumen: 8

Número: 10

Pages: 918-928

Type: Article

DOI: 10.1016/S1474-4422(09)70211-X GOOGLE SCHOLAR lock_openAccès ouvert editor
La source de données: Scopus