Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle

  1. Arechavala-Gomeza, V.
  2. Graham, I.R.
  3. Popplewell, L.J.
  4. Adams, A.M.
  5. Aartsma-Rus, A.
  6. Kinali, M.
  7. Morgan, J.E.
  8. Van Deutekom, J.C.
  9. Wilton, S.D.
  10. Dickson, G.
  11. Muntoni, F.
Aldizkaria:
Human Gene Therapy

ISSN: 1043-0342

Argitalpen urtea: 2007

Alea: 18

Zenbakia: 9

Orrialdeak: 798-810

Mota: Artikulua

DOI: 10.1089/HUM.2006.061 GOOGLE SCHOLAR

Garapen Iraunkorreko Helburuak