TRASTORNOS CONGÉNITOS DEL METABOLISMO
Boston Children's Hospital
Boston, Estados UnidosPublikationen in Zusammenarbeit mit Forschern von Boston Children's Hospital (1)
2019
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International best practice for the evaluation of responsiveness to sapropterin dihydrochloride in patients with phenylketonuria
Molecular Genetics and Metabolism, Vol. 127, Núm. 1, pp. 1-11