TRASTORNOS CONGÉNITOS DEL METABOLISMO
Hospital General Universitario Gregorio Marañón
Madrid, EspañaPublications en collaboration avec des chercheurs de Hospital General Universitario Gregorio Marañón (1)
2018
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Efficacy of Idursulfase therapy in patients with Mucopolysaccharidosis type II who initiated enzyme replacement therapy in adult age. A systematic review of the literature
Molecular Genetics and Metabolism, Vol. 124, Núm. 3, pp. 216-227