PATRICIA
SOBLECHERO MARTÍN
Forscherin bis um 2022
Publikationen, an denen er mitarbeitet PATRICIA SOBLECHERO MARTÍN (6)
2022
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Evaluation of Exon Skipping and Dystrophin Restoration in In Vitro Models of Duchenne Muscular Dystrophy
Methods in Molecular Biology (Humana Press Inc.), pp. 217-233
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Lessons learned from developing an oligonucleotide drug for a rare disease
RNA Therapeutics: The Evolving Landscape of RNA Therapeutics (Elsevier), pp. 121-137
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miR-106b is a novel target to promote muscle regeneration and restore satellite stem cell function in injured Duchenne dystrophic muscle
Molecular Therapy - Nucleic Acids, Vol. 29, pp. 769-786
2021
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Duchenne muscular dystrophy cell culture models created by CRISPR/Cas9 gene editing and their application in drug screening
Scientific Reports, Vol. 11, Núm. 1
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Utrophin modulator drugs as potential therapies for Duchenne and Becker muscular dystrophies
Neuropathology and Applied Neurobiology, Vol. 47, Núm. 6, pp. 711-723
2020
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An overview of alternative splicing defects implicated in myotonic dystrophy type i
Genes, Vol. 11, Núm. 9, pp. 1-27