VIRGINIA
ARECHAVALA GOMEZA
Catholic University of the Sacred Heart
Milán, ItaliaPublikationen in Zusammenarbeit mit Forschern von Catholic University of the Sacred Heart (4)
2016
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Stakeholder cooperation to overcome challenges in orphan medicine development: The example of Duchenne muscular dystrophy
The Lancet Neurology, Vol. 15, Núm. 8, pp. 882-890
2014
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Biochemical characterization of patients with in-frame or out-of-frame DMD deletions pertinent to exon 44 or 45 skipping
JAMA Neurology, Vol. 71, Núm. 1, pp. 32-40
2011
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Dystrophin quantification and clinical correlations in Becker muscular dystrophy: Implications for clinical trials
Brain
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Muscle histology vs MRI in Duchenne muscular dystrophy
Neurology, Vol. 76, Núm. 4, pp. 346-353