Publicaciones en colaboración con investigadores/as de Hospital Universitario de Basurto (4)

2022

  1. Evaluation of Exon Skipping and Dystrophin Restoration in In Vitro Models of Duchenne Muscular Dystrophy

    Methods in Molecular Biology (Humana Press Inc.), pp. 217-233

  2. Lessons learned from developing an oligonucleotide drug for a rare disease

    RNA Therapeutics: The Evolving Landscape of RNA Therapeutics (Elsevier), pp. 121-137

2021

  1. Duchenne muscular dystrophy cell culture models created by CRISPR/Cas9 gene editing and their application in drug screening

    Scientific Reports, Vol. 11, Núm. 1

  2. Utrophin modulator drugs as potential therapies for Duchenne and Becker muscular dystrophies

    Neuropathology and Applied Neurobiology, Vol. 47, Núm. 6, pp. 711-723