Publicaciones en colaboración con investigadores/as de University of Paris-Saclay (5)

2023

  1. Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides

    Nucleic acid therapeutics, Vol. 33, Núm. 1, pp. 1-16

2021

  1. Delivery of oligonucleotide-based therapeutics: challenges and opportunities

    EMBO Molecular Medicine, Vol. 13, Núm. 4

  2. Researcher's Perceptions on Publishing "negative" Results and Open Access

    Nucleic Acid Therapeutics, Vol. 31, Núm. 3, pp. 185-189

2017

  1. Delivery is key: lessons learnt from developing splice-switching antisense therapies

    EMBO Molecular Medicine, Vol. 9, Núm. 5, pp. 545-557

2016

  1. Stakeholder cooperation to overcome challenges in orphan medicine development: The example of Duchenne muscular dystrophy

    The Lancet Neurology, Vol. 15, Núm. 8, pp. 882-890