VIRGINIA
ARECHAVALA GOMEZA
Hammersmith Hospital
Londres, Reino UnidoPublicaciones en colaboración con investigadores/as de Hammersmith Hospital (5)
2011
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Chronic systemic therapy with low-dose morpholino oligomers ameliorates the pathology and normalizes locomotor behavior in mdx mice
Molecular Therapy, Vol. 19, Núm. 2, pp. 345-354
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Muscle histology vs MRI in Duchenne muscular dystrophy
Neurology, Vol. 76, Núm. 4, pp. 346-353
2010
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Revertant fibres and dystrophin traces in Duchenne muscular dystrophy: Implication for clinical trials
Neuromuscular Disorders, Vol. 20, Núm. 5, pp. 295-301
2009
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Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study
The Lancet Neurology, Vol. 8, Núm. 10, pp. 918-928
2007
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Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle
Human Gene Therapy, Vol. 18, Núm. 9, pp. 798-810