VIRGINIA
ARECHAVALA GOMEZA
University of Oxford
Oxford, Reino UnidoPublikationen in Zusammenarbeit mit Forschern von University of Oxford (5)
2021
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Delivery of oligonucleotide-based therapeutics: challenges and opportunities
EMBO Molecular Medicine, Vol. 13, Núm. 4
2017
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Delivery is key: lessons learnt from developing splice-switching antisense therapies
EMBO Molecular Medicine, Vol. 9, Núm. 5, pp. 545-557
2016
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Stakeholder cooperation to overcome challenges in orphan medicine development: The example of Duchenne muscular dystrophy
The Lancet Neurology, Vol. 15, Núm. 8, pp. 882-890
2011
2009
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Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study
The Lancet Neurology, Vol. 8, Núm. 10, pp. 918-928