VIRGINIA
ARECHAVALA GOMEZA
University of Western Australia
Perth, AustraliaPublications en collaboration avec des chercheurs de University of Western Australia (4)
2011
2010
-
Comparative analysis of antisense oligonucleotide sequences targeting exon 53 of the human DMD gene: Implications for future clinical trials
Neuromuscular Disorders, Vol. 20, Núm. 2, pp. 102-110
2009
-
Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study
The Lancet Neurology, Vol. 8, Núm. 10, pp. 918-928
2007
-
Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle
Human Gene Therapy, Vol. 18, Núm. 9, pp. 798-810