PATRICIA
SOBLECHERO MARTÍN
Chercheuse jusqu' 2022
Hospital Universitario de Basurto
Bilbao, EspañaPublications en collaboration avec des chercheurs de Hospital Universitario de Basurto (4)
2022
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Evaluation of Exon Skipping and Dystrophin Restoration in In Vitro Models of Duchenne Muscular Dystrophy
Methods in Molecular Biology (Humana Press Inc.), pp. 217-233
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Lessons learned from developing an oligonucleotide drug for a rare disease
RNA Therapeutics: The Evolving Landscape of RNA Therapeutics (Elsevier), pp. 121-137
2021
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Duchenne muscular dystrophy cell culture models created by CRISPR/Cas9 gene editing and their application in drug screening
Scientific Reports, Vol. 11, Núm. 1
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Utrophin modulator drugs as potential therapies for Duchenne and Becker muscular dystrophies
Neuropathology and Applied Neurobiology, Vol. 47, Núm. 6, pp. 711-723