MARCOS JESÚS
ARAÚZO BRAVO
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Erasmus University Medical Center
Róterdam, HolandaPublicaciones en colaboración con investigadores/as de Erasmus University Medical Center (1)
2017
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GAA Deficiency in Pompe Disease Is Alleviated by Exon Inclusion in iPSC-Derived Skeletal Muscle Cells
Molecular Therapy - Nucleic Acids, Vol. 7, pp. 101-115